Viral vectors expressing proneural genes can stimulate adult mammalian retinal glia to become immature neurons. These glia-derived neurons share properties with the bipolar, amacrine and retinal ...
BARCELONA, Spain I March 13, 2025 I SpliceBio, a clinical-stage genetic medicines company pioneering Protein Splicing to address diseases caused by mutations ...
Right now, the IND-enabling studies are made to test the safety, tolerability, vector biodistribution, transgene expression, ...
In the phase 1/2 INSPIRE DUCHENNE trial, interim data showed an average microdystrophin expression of 110% among participants ...
The National Institute for Innovation in Manufacturing Biopharmaceuticals (NIIMBL) is pleased to announce a Request for ...
Amazon S3 on MSN24d
AAV Innovation Summit 2025 to Explore AI and Vector Design in Gene TherapyThe AAV Innovation Summit 2025, hosted by Form Bio, will bring together top experts in gene therapy to discuss the latest advancements in adeno-associated virus (AAV) therapeutics. The event, set for ...
AI-assisted AAV capsid engineering has transformative potential in terms of accelerating and optimizing the development of gene therapies.
Avirmax Biopharma Inc. has begun IND-enabling studies of ABI-201, a gene therapy for dry age-related macular degeneration ...
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